Sponsor Overview
Explore verified public information about Children's Hospital of Philadelphia's expanded access programs, compassionate use policies, and patient eligibility pathways. This report aggregates official statements, independent research, and regulatory data to help patients, providers, and sponsors collaborate efficiently.
Unique references curated across 4 content categories.
ClinicalTrials.gov data sources power this status.
Dataset refreshed continuously through Right2Hope ETL pipelines.
Expanded Access Intelligence
Official Statements
Score contribution: 100 — 1 supporting sources.
“The Suzi and Scott Lustgarten Center for GI Motility at Children’s Hospital of Philadelphia (CHOP) offers cisapride and domperidone through expanded access programs.”
Active EAPs on ClinicalTrials.gov
Score contribution: 60 — 2 supporting sources.
Conditions: Congenital Hyperinsulinism (CHI), Beckwith-Wiedemann Syndrome, Insulinoma
Conditions: Leukemia, Bone Marrow Failure Syndrome, Immunodeficiencies
Past EAPs on ClinicalTrials.gov
Score contribution: 40 — 2 supporting sources.
Conditions: Cholestasis, Short Bowel Syndrome
Conditions: Iron Overload
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